Lv6
1950 积分 2023-10-07 加入
An RNA editing strategy rescues gene duplication in a mouse model of MECP2 duplication syndrome and nonhuman primates
11天前
已完结
Autism-like behaviours and germline transmission in transgenic monkeys overexpressing MeCP2
11天前
已完结
Whole-brain in vivo base editing reverses behavioral changes in Mef2c-mutant mice
11天前
已完结
Direct Dorsal Root Ganglia (DRG) Injection in mice for Analysis of Adeno-associated Viral (AAV) Gene Transfer to Peripheral Somatosensory Neurons
1个月前
已完结
Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C)
3个月前
已关闭
Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C)
3个月前
已完结
Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C)
3个月前
已完结
Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C)
3个月前
已关闭
AAV-RNAi constructs promote DRG toxicity
3个月前
已完结
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