Lv1
30 积分 2023-01-24 加入
Antisense oligonucleotides: the next frontier for treatment of neurological disorders
18小时前
待确认
Challenges and opportunities in spinal muscular atrophy therapeutics
6天前
已完结
Amino acid supplementation enhances in vivo efficacy of lipid nanoparticle–mediated mRNA delivery in preclinical models
7天前
已完结
Hepatic glycogenesis antagonizes lipogenesis by blocking S1P via UDPG
19天前
已完结
Brain-targeted co-delivery of therapeutic gene and peptide by multifunctional nanoparticles in Alzheimer's disease mice
1个月前
已完结
Analyzing Endolysosome–Mitochondria Membrane Contact Sites by Thin Section TEM of Human Fibroblasts
3个月前
已完结
The evolving landscape of spinal muscular atrophy treatment
4个月前
已完结
Author Correction: AAV-based delivery of RNAi targeting ataxin-2 improves survival and pathology in TDP-43 mice
4个月前
已完结
AAV-Mediated Exon Skipping Therapy for Usher Syndrome, Type 2A
4个月前
已完结
Counteracting chromatin effects of a splicing-correcting antisense oligonucleotide improves its therapeutic efficacy in spinal muscular atrophy
6个月前
已完结