Lv2
170 积分 2025-03-12 加入
Generation of tumor neoantigens by RNA splicing perturbation
7天前
已完结
In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates
2个月前
已完结
Phase 1 First-in-Human Dose-Expansion Study of The Oral SF3B1 Modulator H3B‑8800 In Lower-Risk Myelodysplastic Syndrome
2个月前
已完结
Real-world evidence on nusinersen treatment of persons with SMA: a focused review
2个月前
已完结
Involvement of U6 snRNA in 5′ Splice Site Selection
2个月前
已完结
Overexpression of adapted U1snRNA in patients' cells to correct a 5′ splice site mutation in propionic acidemia
2个月前
已完结
The mutational spectrum of single base-pair substitutions in mRNA splice junctions of human genes: Causes and consequences
2个月前
已完结
Locked vs. unlocked nucleic acids (LNA vs. UNA): contrasting structures work towards common therapeutic goals
2个月前
已完结
2-Modified Oligonucleotides for Antisense Therapeutics
2个月前
已完结
Cellular uptake and trafficking of antisense oligonucleotides
2个月前
已完结