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190 积分 2025-03-12 加入
Programmable RNA editing with compact CRISPR–Cas13 systems from uncultivated microbes
9小时前
待确认
Antisense technology: an overview and prospectus
13小时前
已完结
CLUSTER guide RNAs enable precise and efficient RNA editing with endogenous ADAR enzymes in vivo
16小时前
已完结
Antisense oligonucleotides increase Scn1a expression and reduce seizures and SUDEP incidence in a mouse model of Dravet syndrome
9天前
已完结
Generation of tumor neoantigens by RNA splicing perturbation
20天前
已完结
In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates
2个月前
已完结
Phase 1 First-in-Human Dose-Expansion Study of The Oral SF3B1 Modulator H3B‑8800 In Lower-Risk Myelodysplastic Syndrome
2个月前
已完结
Real-world evidence on nusinersen treatment of persons with SMA: a focused review
2个月前
已完结
Involvement of U6 snRNA in 5′ Splice Site Selection
3个月前
已完结
Overexpression of adapted U1snRNA in patients' cells to correct a 5′ splice site mutation in propionic acidemia
3个月前
已完结
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