Lv33
280 积分 2025-08-21 加入
Mitochondrial gene editing
1小时前
已完结
A phase 1/2 study of LY3884961 (PR001) an AAV9-based gene therapy for Gaucher disease type 2 – A clinical update from the PROVIDE trial
12天前
已关闭
Quick tips for interpreting cell death experiments
13天前
已完结
Robust scoring of selective drug responses for patient-tailored therapy selection
15天前
已完结
Gaucher disease provides a unique window into Parkinson disease pathogenesis
19天前
已完结
Efficient mitochondrial A-to-G base editors for the generation of mitochondrial disease models
27天前
已完结
Precise modelling of mitochondrial diseases using optimized mitoBEs
1个月前
已完结
Structure-guided AAV capsid evolution strategies for enhanced CNS gene delivery
1个月前
已完结
Dual AAV vectors for efficient delivery of large transgenes
1个月前
已完结
Decoding human chemical reprogramming: mechanisms and principles
2个月前
已完结