Lv1
90 积分 2023-10-01 加入
New evidence on the clinical, genetic, and biochemical bases of GBA1-Parkinson’s disease: prospects for treatment
12天前
已关闭
Oligodendrocyte-targeted adeno-associated virus gene therapy for Canavan disease in children: a phase 1/2 trial
1个月前
已完结
Semiquantitative Scale for Assessing Brain MRI Abnormalities in Wilson Disease: A Validation Study
1个月前
已完结
Neurofilaments as biomarkers in neurological disorders - towards clinical application
1个月前
已完结
Serum Neurofilament Light Chain as a Biomarker of Brain Injury in Wilson's Disease: Clinical and Neuroradiological Correlations
1个月前
已完结
AAV gene therapy for autosomal recessive deafness 9: a single-arm trial
1个月前
已完结
In vivo base editing gene therapy for heterozygous familialhypercholesterolemia:a phaseItrial
1个月前
已完结
AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial
2个月前
已完结
Clinical consequences of interrupting enzyme replacement therapy in children with type 1 Gaucher disease
3个月前
已完结
In vivo chimeric antigen receptor (CAR)-T cell therapy
3个月前
已完结