Lv1
70 积分 2023-04-02 加入
Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease
1个月前
已完结
Transduction of Quiescent Human Hematopoietic Stem and Progenitor Cells Using Lentiviral Vectors and Virus‐Like Particles
1个月前
已完结
CONGENITAL DOPAMINE-BETA-HYDROXYLASE DEFICIENCY
1个月前
已关闭
Clinical application of base editing for treating β-thalassaemia
2个月前
已完结
Toxicity Analysis of Busulfan Pharmacokinetic Guided Therapeutic Dose Monitoring for Myeloablative Conditioning Regimens with Allogeneic Transplantation
3个月前
已完结
Zycubo (copper histidinate), the first treatment for pediatric Menkes disease
3个月前
已关闭
The Cell and Gene Therapy Access Model — A Vision for Future Development
3个月前
已完结
One Pivotal Trial, the New Default Option for FDA Approval — Ending the Two-Trial Dogma
4个月前
已完结
Standardising busulfan dosage for children and young adults
5个月前
已完结
First-Line Unrelated Double-Unit Umbilical Cord Blood Transplantation for Acquired Severe Aplastic Anemia
6个月前
已完结