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70 积分 2025-05-01 加入
Enhanced genome editing to ameliorate a genetic metabolic liver disease through co-delivery of adeno-associated virus receptor
3天前
已完结
Recovery of neurogenic amines in phenylketonuria mice after liver-targeted gene therapy
21天前
已完结
Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice
21天前
已完结
Increasing intracellular dNTP levels improves prime editing efficiency
1个月前
已完结