Lv1
20 积分 2025-11-04 加入
AAV-mediated FGF21 gene therapy promotes health span extension by whole-body tissue-specific adaptations
1个月前
已完结
Successful In Vitro Modification of the Dmd Gene Using Prime Editing
3个月前
已完结
Enhancing KLF15 activity in cardiomyocytes: a novel approach to prevent pathological reprogramming and fibrosis via nuclease-deficient dCas9VPR
5个月前
已完结
An engineered UGA suppressor tRNA gene for disease-agnostic AAV delivery
7个月前
已完结
Therapeutic Modulation of DMD Splicing by Blocking Exonic Splicing Enhancer Sites with Antisense Oligonucleotides
7个月前
已完结
Efficient exon skipping by base-editor-mediated abrogation of exonic splicing enhancers
8个月前
已完结
Efficient exon skipping by base-editor-mediated abrogation of exonic splicing enhancers
8个月前
已完结
Prime editing-installed suppressor tRNAs for disease-agnostic genome editing
9个月前
已完结
Mouse model carrying H222P- Lmna mutation develops muscular dystrophy and dilated cardiomyopathy similar to human striated muscle laminopathies
9个月前
已完结
Genotype-phenotype associations in dilated cardiomyopathy: meta-analysis on more than 8000 individuals
9个月前
已完结