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Enhancing KLF15 activity in cardiomyocytes: a novel approach to prevent pathological reprogramming and fibrosis via nuclease-deficient dCas9VPR
4天前
已完结
An engineered UGA suppressor tRNA gene for disease-agnostic AAV delivery
1个月前
已完结
Therapeutic Modulation of DMD Splicing by Blocking Exonic Splicing Enhancer Sites with Antisense Oligonucleotides
2个月前
已完结
Efficient exon skipping by base-editor-mediated abrogation of exonic splicing enhancers
2个月前
已完结
Efficient exon skipping by base-editor-mediated abrogation of exonic splicing enhancers
2个月前
已完结
Prime editing-installed suppressor tRNAs for disease-agnostic genome editing
3个月前
已完结
Mouse model carrying H222P- Lmna mutation develops muscular dystrophy and dilated cardiomyopathy similar to human striated muscle laminopathies
3个月前
已完结
Genotype-phenotype associations in dilated cardiomyopathy: meta-analysis on more than 8000 individuals
3个月前
已完结
Discovery and Engineering of Retrons for Precise Genome Editing
4个月前
已完结
LMNA-related cardiomyopathy: From molecular pathology to cardiac gene therapy
4个月前
已完结