Lv69
2218 积分 2024-04-15 加入
Myotonic dystrophy type 1 – updates on mechanisms of multisystemic manifestations, genetically targeted therapeutics, and preparing for a postapproval world
30分钟前
求助中
Iptacopan in IgA Nephropathy — Final 24-Month Data
48分钟前
已完结
Gene Editing, Peroxisomal Disorders, and Treatments for Rare Disease
1小时前
已完结
Genome-wide association analyses of gestational phenotypes identify context-specific genetic effects
4小时前
已完结
More muscle, less belly fat: mutations to a gene are linked to wide-ranging benefits
13天前
已完结
Integrative exome sequencing and multi-omics analysis elucidates the regulatory role of rare variants in metabolic syndrome
27天前
已完结
Efficacy and Safety of Obinutuzumab in Active Systemic Lupus Erythematosus
28天前
已完结
Longer-Term Efficacy and Safety of Zodasiran in Patients with Mixed Hyperlipidaemia
28天前
已完结
Cliramitug for depletion of cardiac amyloid transthyretin: long-term follow-up of the NI006-101 trial
1个月前
已完结
A new era for myotonic dystrophy: Improved delivery of a DMPK-targeted oligonucleotide modulates muscle transcriptomes and function
1个月前
已完结