Lv1
50 积分 2025-08-27 加入
Outcomes of an optimized ciclosporin‐free haploidentical HSCT protocol in paediatric patients with cerebral adrenoleukodystrophy
5天前
已关闭
Consensus Guidelines for Imaging in Adrenoleukodystrophy
8天前
已完结
Allogeneic Stem Cell Transplant for Cerebral Adrenoleukodystrophy: The Changing Role of Alternative Donors
1个月前
已关闭
A pilot study of newborn screening for X-linked adrenoleukodystrophy based on liquid chromatography-tandem mass spectrometry method for detection of C26:0-lysophosphatidylcholine in dried blood spots: Results from 43,653 newborns in a southern Chinese population
2个月前
已完结
GJB2 p.V37I Mutation Associated With Moderate Nonsyndromic Hearing Loss in an Adult Taiwanese Population
4个月前
已完结
Erucic Acid: A Possible Therapeutic Agent for Neurodegenerative Diseases
4个月前
已完结
Review of the potential pharmacological role of erucic acid: a monounsaturated omega-9 fatty acid
4个月前
已完结
Accelerated Course of Cerebral Adrenoleukodystrophy After Coronavirus Disease 2019 Infection
4个月前
已完结
Phase I clinical trial of intracerebral injection of lentiviral-ABCD1 for the treatment of cerebral adrenoleukodystrophy
4个月前
已完结
Intracerebral lentiviral ABCD1 gene therapy in an early disease onset ALD mouse model
4个月前
已完结