Lv1
60 积分 2026-07-07 加入
Durability of CRISPR-Cas9 Gene Editing Targeting ANGPTL3 with CTX310
1个月前
已完结
Cell-penetrating asymmetric siRNA targeting MyD88 suppresses inflammasome-driven ocular degeneration and angiogenesis
1个月前
已完结
miR-375 protects against acetaminophen-induced acute liver failure by orchestrating pharmacogene expression
1个月前
已完结
Reduction of arthritis following intra-articular administration of an adeno-associated virus serotype 5 expressing a disease-inducible TNF-blocking agent
1个月前
已完结
Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS
1个月前
已完结
Treatment of spinal injury muscle spasticity by spinal subpial AAV9-GAD65/VGAT delivery: an efficacy and safety study in rat, pig and NHP
1个月前
已完结
Cell-penetrating asymmetric siRNA targeting MyD88 suppresses inflammasome-driven ocular degeneration and angiogenesis
1个月前
已完结
Efficient and modified 2-NBDG assay to measure glucose uptake in cultured myotubes
1个月前
已完结
AAVLINK: A potent DNA-recombination method for large cargo delivery in gene therapy
2个月前
已完结