Lv11
80 积分 2025-05-14 加入
Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndrome
55分钟前
已完结
Phosphoproteomics Profiling Reveals Key Proteins Involved in Neuroinflammation and Impaired Axon Guidance Induced by Bilirubin Deficiency
3个月前
已完结
Clinical practice guidelines for gene therapy to treat hereditary hearing loss
3个月前
已完结
Precise and efficient DNA base editing restores normal hearing in adult DFNB9 mouse model
4个月前
已完结
Precise and efficient DNA base editing restores normal hearing in adult DFNB9 mouse model
5个月前
已完结
Late-onset riboflavin transporter deficiency: a treatable mimic of various motor neuropathy aetiologies
6个月前
已完结
The audiovestibular profile of Brown-Vialetto-Van Laere syndrome
6个月前
已完结
Ocular Biomarkers of Riboflavin Transporter Deficiency
6个月前
已关闭
Child Neurology: Five-Year Update on Siblings With Riboflavin Transporter Deficiency: Stable Visual and Neurologic Status With Continued Riboflavin Therapy
6个月前
已完结
DB-OTO Gene Therapy for Inherited Deafness
8个月前
已完结