Lv33
201 积分 2022-02-16 加入
Preclinical Evaluation of AAV8-R338L Gene Therapy for Hemophilia: Efficacy, Pharmacokinetics, Distribution, Excretion and Toxicity in Mouse Models and Non-human Primates
2小时前
求助中
Evaluation of the Humoral Response to Adeno-Associated Virus-Based Gene Therapy Modalities Using Total Antibody Assays
5小时前
已完结
AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial
16天前
已完结
Mini review: Gene therapy targets for aging-associated diseases
16天前
已完结
Klotho attenuates D-galactose-induced cardiac aging through the ROS/NLRP3/pyroptosis pathway
18天前
已完结
WDR45 deficiency shortens axon length in dopaminergic neurons from patient-derived iPSCs
19天前
已完结
Early Intervention with Intravenous AAV9 Gene Therapy Significantly Improves Biomarkers and Phenotypes in a Floxed Mouse Model of X-linked Alport Syndrome
20天前
已关闭
Improving AAV8 purification with continuous affinity capture: from batch to continuous multicolumn chromatography
21天前
已完结
AAV9‐DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice
21天前
已完结
CRISPR activation for SCN2A-related neurodevelopmental disorders
22天前
已完结
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