Lv7
3350 积分 2022-12-16 加入
A tetramer of BCL11A is required for stable protein production and fetal hemoglobin silencing
5天前
已完结
Single-cell profiling of human bone marrow progenitors reveals mechanisms of failing erythropoiesis in Diamond-Blackfan anemia
19天前
已完结
两例2p15-p16.1微缺失综合征的产前诊断
26天前
已完结
Unlocking biological barriers: nonclinical safety considerations for RNA-based complex biologics
28天前
已完结
Developing a pill to treat sickle cell disease
29天前
已完结
Molecular glue degrader for sickle cell disease
29天前
已完结
A molecular glue degrader of the WIZ transcription factor for fetal hemoglobin induction
29天前
已完结
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat β-Thalassemia
29天前
已完结
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease
29天前
已完结
Safety and efficacy of hemobeglogene autotemcel(hemo-cel) gene therapy in five patients with transfusion-dependent β-thalassemia
29天前
已完结
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