Lv1
70 积分 2025-03-04 加入
Transient muscle expression of mitoARCUS in mice leads to a sustained reduction in pathogenic mtDNA content and improves muscle function
13天前
已完结
Development of dual base editors based on ssDNA-targeting SCP1.201 deaminases for the artificial evolution of novel herbicide-tolerance OsEPSPS variants
1个月前
已完结
Combined AAV-mediated specific Gjb2 expression restores hearing in DFNB1 mouse models
1个月前
已完结
A Novel Delivery Approach of Clinical Inner Ear Gene Therapy
1个月前
已完结
Clinical gene therapy restores hearing: a paradigm shift
1个月前
已完结
AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial
1个月前
已完结
Intracerebral gene therapy in children with metachromatic leukodystrophy: Results of a phase I/II trial
2个月前
已完结
A Comprehensive Atlas of AAV Tropism in the Mouse
2个月前
已完结
An AAV variant selected through NHP screens robustly transduces the brain and drives secreted protein expression in NHPs and mice
2个月前
已完结
Identification and Phylogenetic Characterisation of Novel Adeno‐Associated Virus Capsids in Non‐Human Primate Tissues
3个月前
已完结