Lv21
148 积分 2025-09-18 加入
Targeted genome editing of ZKSCAN3 mitigates the neurotoxicity caused by mutant HTT (huntingtin) in a Huntington disease animal model and three-dimensional cell culture of Huntington disease
2个月前
已完结
Biomembrane-inspired lipid nanoparticles enhance CRISPR-Cas9 editing for hemophilia A
2个月前
已关闭
Genome engineering with Cas9 and AAV repair templates generates frequent concatemeric insertions of viral vectors
2个月前
已完结
CRISPR targeting of mmu-miR-21a through a single adeno-associated virus vector prolongs survival of glioblastoma-bearing mice
2个月前
已完结
Liver-directed AAV gene therapy normalizes disease symptoms and provides cross-correction in a mouse model of lysosomal acid lipase deficiency
2个月前
已完结
Adeno-associated viral vector targeted evolution for neurofibromatosis gene delivery
2个月前
已完结
In vivo engineering of murine T cells using the evolved adeno-associated virus variant Ark313
2个月前
已完结
Engineering sialylated N-glycans on adeno-associated virus capsids for targeted gene delivery and therapeutic applications
2个月前
已完结
BMP4-GPX4 can improve the ferroptosis phenotype of retinal ganglion cells and enhance their differentiation ability after retinal stem cell transplantation in glaucoma with high intraocular pressure
2个月前
已完结
MXene-Chitosan Photo-Responsive Conduit for Wireless Optogenetic Stimulation to Enhance Neural Regeneration and Functional Recovery after Optic Nerve Injury
2个月前
已完结