Lv1
68 积分 2025-08-28 加入
Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans
4天前
已完结
AAVLINK: A potent DNA-recombination method for large cargo delivery in gene therapy
4个月前
已完结
α-Actinin-2 in rat striatum: localization and interaction with NMDA glutamate receptor subunits
5个月前
已完结
Phenylbutyrate Ameliorates Cognitive Deficit and Reduces Tau Pathology in an Alzheimer's Disease Mouse Model
5个月前
已完结
Interneuron-specific dual-AAV SCN1A gene replacement corrects epileptic phenotypes in mouse models of Dravet syndrome
5个月前
已完结
AAV-based in vivo gene therapy for neurological disorders
6个月前
已完结
Long-read sequencing and profiling of RNA-binding proteins reveals the pathogenic mechanism of aberrant splicing of anSCN1Apoison exon in epilepsy
6个月前
已关闭
Near-cognate tRNAs increase the efficiency and precision of pseudouridine-mediated readthrough of premature termination codons
6个月前
已完结
Barcoding Notch signaling in the developing brain
8个月前
已完结
Prime editing using CRISPR-Cas12a and circular RNAs in human cells
9个月前
已完结
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