Lv51
1570 积分 2023-05-12 加入
A Gene, A Breakthrough, A Challenge: Lessons From the History of Spinal Muscular Atrophy
1个月前
已完结
Urine protein/osmolality and creatinine/osmolality ratios for assessing proteinuria and motor function in children with spinal muscular atrophy
1个月前
已完结
Immediate Risdiplam Bridging after Diagnosis and Prior to Onasemogene Abaparvovec in SMA with Two SMN2 Copies: Real World Evidence from an Observational National Cohort Study
1个月前
已关闭
Multiple spinal muscular atrophy disease-modifying effects of a Hspa8G470R synaptic chaperone variant
1个月前
已关闭
Medication Usage in Motor Neuron Disease and Spinal Muscular Atrophy: Insights from the Muscular Dystrophy Association Neuromuscular Observational Research Data Hub
1个月前
已完结
Beyond Survival: Parenting and Psychosocial Support in the New Era of Spinal Muscular Atrophy
1个月前
已完结
Determinants of hepatic enzyme elevations following onasemnogene abeparvovec: Results from a unified immunomodulation protocol
1个月前
已完结
Polysomnographic Characteristics in Children with Spinal Muscular Atrophy Compared to Healthy Children: A Retrospective Analysis
2个月前
已关闭
Insights From Wise Warriors: A Needs Assessment and Preventive Parenting Program Recommendations From Parents of Children With Spinal Muscular Atrophy
2个月前
已关闭
Treatment Preferences in Adult Patients with Type 2 and Type 3 Spinal Muscular Atrophy: Evidence from a Discrete Choice Experiment in China
2个月前
已完结
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