Lv13
30 积分 2026-01-07 加入
Efficacy and safety of nipocalimab in patients with moderate-to-severe Sjögren's disease (DAHLIAS): a randomised, phase 2, placebo-controlled, double-blind trial
1天前
已完结
Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency
2天前
已完结
Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B
2天前
已完结
An Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II
2天前
已完结