Lv21
142 积分 2022-10-31 加入
Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndrome
9天前
已完结
Intravitreal Delivery of rAAV2tYF-CB-hRS1 Vector for Gene Augmentation Therapy in Patients with X-Linked Retinoschisis
12天前
已完结
Biotech financing: darkest before the dawn
15天前
已完结
Successful AAV8 readministration: Suppression of capsid‐specific neutralizing antibodies by a combination treatment of bortezomib and CD20 mAb in a mouse model of Pompe disease
1个月前
已完结
Recent endeavors in MECP2 gene transfer for gene therapy of Rett syndrome
1个月前
已关闭
皮肤病受累面积和外用药用量的计算方法
2个月前
已关闭
Prevalence of Neutralizing Antibodies Against AAV Serotypes 2 and 9 in Healthy Participants from Multiple Centers Across China and Patients with DMD/BMD
2个月前
已完结
Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C)
3个月前
已完结
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