Lv2
130 积分 2025-12-16 加入
In vivo genome editing of human haematopoietic stem cells for treatment of blood disorders using mRNA delivery
3个月前
已完结
Effective Gene Therapy for Hemophilia a: Novel Re-Dosable Non-Viral Formulation That Provides Stable, and Durable FVIII Expression with Improved Tolerability
3个月前
已关闭
Flow Cytometry Assay to Monitor Effectiveness of Gene Therapy Correction in Peripheral Blood Mononuclear Cells of Gaucher Disease Type I Patients
4个月前
已关闭