Lv63
1920 积分 2024-10-21 加入
Microglial TMEM119 binds to amyloid-β to promote its clearance in an Aβ-depositing mouse model of Alzheimer’s disease
1个月前
已完结
Transferrin receptor–targeted anti-amyloid antibody enhances brain delivery and mitigates ARIA
2个月前
已完结
Engineered Un1Cas12f1 with boosted gene-editing activity and expanded genomic coverage
2个月前
已完结
In vivo engineering of murine T cells using the evolved adeno-associated virus variant Ark313
2个月前
已完结
AAV-delivered PPT1 provides long-term neurological benefits in CLN1 mice and achieves therapeutic levels in sheep brain
2个月前
已完结
Buffer Valency Engineering Enables High-concentration and Shelf-stable DNA Transfection Particles for Viral Vector Production
2个月前
已完结
Targeting microRNA-dependent control of X chromosome inactivation improves the Rett Syndrome phenotype
3个月前
已完结
AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models
3个月前
已完结
Formulation Development and Feasibility of AAV5 as a Lyophilized Drug Product
3个月前
已完结
Blood–brain-barrier-crossing lipid nanoparticles for mRNA delivery to the central nervous system
3个月前
已完结