Lv11
38 积分 2024-05-10 加入
AAV gene therapy for homozygous familial hypercholesterolemia: a phase 1 trial
3小时前
待确认
Anti-neutrophil cytoplasmic antibody-associated vasculitis: biological insights and biomarker-guided disease management
9天前
已完结
High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injury
30天前
已完结
Structure and function of polycystins: insights into polycystic kidney disease
1个月前
已完结
Optimizing Peptide Ionizable Lipids Enables Efficient and Low‐Toxicity mRNA Delivery for In Vivo Prime Editing and Protein Replacement Therapy
1个月前
已完结
Global perspective of familial hypercholesterolaemia: a cross-sectional study from the EAS Familial Hypercholesterolaemia Studies Collaboration (FHSC)
4个月前
已完结
Familial hypercholesterolaemia in children and adolescents from 48 countries: a cross-sectional study
4个月前
已完结
Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3
4个月前
已完结
Zodasiran, an RNAi therapeutic targeting ANGPTL3, for treating patients with homozygous familial hypercholesterolaemia (GATEWAY): an open-label, randomised, phase 2 trial
4个月前
已完结
Efficacy and safety of inclisiran in adolescents with heterozygous familial hypercholesterolaemia (ORION-16): a two-part, randomised, multicentre clinical trial
4个月前
已完结