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30 积分 2026-08-05 加入
Natural history of a cohort of children with type 2 spinal muscular atrophy from southern India - A retrospective single-centre study
3小时前
待确认
Gain and loss of abilities in type II SMA: A 12-month natural history study
9小时前
已完结
Age and baseline values predict 12 and 24-month functional changes in type 2 SMA
3天前
已关闭
Natural history of a cohort of children with type 2 spinal muscular atrophy from southern India - A retrospective single-centre study
9天前
已完结
An international consensus approach to the management of atypical hemolytic uremic syndrome in children
20天前
已完结
Genetic susceptibility to thrombotic microangiopathy in a 10-month-old patient with SMA type 1: a caveat for gene therapy eligibility
20天前
已完结
Neuroepithelial Tumor with AAV Integration after Intracisternal Magna Vector Delivery
1个月前
已完结
Thrombotic microangiopathy following gene therapy for 5q-spinal muscular atrophy
1个月前
已完结
A Review of the Challenge of Pre-Existing Humoral Immunity in Adeno-Associated Virus Gene Therapy and Potential Solutions
1个月前
已完结
Thrombotic Microangiopathy Associated with Systemic Adeno-Associated Virus Gene Transfer: Review of Reported Cases
1个月前
已完结