Lv31
238 积分 2026-05-07 加入
Pharmacology and toxicology of eteplirsen and SRP-5051 for DMD exon 51 skipping: an update
4天前
已完结
Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial
8天前
已完结
Abnormal sodium current properties contribute to cardiac electrical and contractile dysfunction in a mouse model of myotonic dystrophy type 1
14天前
已完结
1-month versus 12-month dual antithrombotic therapy after percutaneous coronary intervention in patients with atrial fibrillation (OPTIMA-AF): a multicentre, open-label, hybrid non-inferiority and superiority, randomised, controlled trial
15天前
已完结
Implications of the 2026 Dyslipidemia Guideline for Primary Prevention Statin Therapy
15天前
已完结
RModBlock antisense oligonucleotides as a universal tool for precise and efficient inhibition of RNA modifications
17天前
已完结
Translation efficiency of mRNAs is increased by antisense oligonucleotides targeting upstream open reading frames
22天前
已完结
Dynamins in human diseases: differential requirement of dynamin activity in distinct tissues
23天前
已完结
Antisense oligonucleotide targeting DMPK in patients with myotonic dystrophy type 1: a multicentre, randomised, dose-escalation, placebo-controlled, phase 1/2a trial
24天前
已完结
Enhanced Delivery of Ligand-Conjugated Antisense Oligonucleotides (C16-HA-ASO) Targeting Dystrophia Myotonica Protein Kinase Transcripts for the Treatment of Myotonic Dystrophy Type 1
1个月前
已完结