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110 积分 2025-04-07 加入
Neuroepithelial Tumor with AAV Integration after Intracisternal Magna Vector Delivery
4天前
已完结
Practical Interpretation of Equivalent Acceptance Criteria
13天前
已完结
Assessing Hybridization-Dependent Off-Target Risk for Therapeutic Oligonucleotides: Updated Industry Recommendations
1个月前
已完结
Multivalent N-Acetylgalactosamine-Conjugated siRNA Localizes in Hepatocytes and Elicits Robust RNAi-Mediated Gene Silencing
1个月前
已完结
An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia
1个月前
已完结
Mechanistic Modeling to Support Hemostatic Equivalency of Antithrombin Lowering in People with Hemophilia A or B
1个月前
已关闭
An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia
1个月前
已完结
Seroprevalence of anti-AAV antibodies in a healthy adult Spanish population: findings from the SAAVIA study
2个月前
已完结
AAVLINK: A potent DNA-recombination method for large cargo delivery in gene therapy
4个月前
已完结
A largely random AAV integration profile after LPLD gene therapy
4个月前
已完结