Lv1
38 积分 2022-12-07 加入
Chromatin remodeling in pericentral hepatocytes modulates MASH through CYP450 activity
4天前
已完结
Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy
4天前
已完结
CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia
4天前
已完结
CRISPR-Cas9 In Vivo Gene Editing of KLKB1 for Hereditary Angioedema
4天前
已完结
CRISPR-Based Therapy for Hereditary Angioedema
4天前
已完结
In vivo adenine base editing ameliorates Dravet syndrome phenotypes in a mouse model
4天前
已完结
AAV8 gene therapy and dietary insults together precipitate cholestatic liver disease in a mouse model of X-linked myotubular myopathy
4天前
已完结
Thrombotic Microangiopathy Associated with Systemic Adeno-Associated Virus Gene Transfer: Review of Reported Cases
4天前
已完结
Gene therapy with covalently closed-end AAV vector for spinal muscular atrophy
4天前
已完结
Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B
4天前
已完结