Lv5
1510 积分 2024-11-21 加入
dCas9-VPR-mediated transcriptional activation of functionally equivalent genes for gene therapy
3个月前
已完结
Efficacy and Safety in 15 Hemophilia B Patients Treated with the AAV Gene Therapy Vector Fidanacogene Elaparvovec and Followed for at Least 1 Year
3个月前
已关闭
Loss of MFE-2 impairs microglial lipid homeostasis and drives neuroinflammation in Alzheimer’s pathogenesis
4个月前
已完结
Recommendations for the Development of Cell-Based Anti-Viral Vector Neutralizing Antibody Assays
5个月前
已完结
Goats with low levels of AAV antibody may serve as candidates for large animal gene therapy
5个月前
已完结
Label-free cell based impedance measurements of ZnO nanoparticles—human lung cell interaction: a comparison with MTT, NR, Trypan blue and cloning efficiency assays
5个月前
已关闭
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery
10个月前
已完结
Immunosuppression Modulates Immune Responses to AAV Capsid in Human Subjects Undergoing Intramuscular Gene Transfer for Lipoprotein Lipase Deficiency
10个月前
已关闭
An International Epidemiology Study to Determine the Prevalence of Preexisting Cell-Mediated Immunity to Adeno-Associated Virus (AAV) in Adults with Severe Hemophilia
10个月前
已关闭