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50 积分 2024-05-10 加入
Model‐Informed Approaches and Innovative Clinical Trial Design for Adeno‐Associated Viral Vector‐Based Gene Therapy Product Development: A White Paper
1天前
待确认
Quantitative Systems Pharmacology Modeling of Adeno-Associated Virus Gene Therapies: Mechanistic Identification of Species-Translation Using Preclinical and Clinical Data
8天前
已完结
PK/PD and Bioanalytical Considerations of AAV-Based Gene Therapies: an IQ Consortium Industry Position Paper
11天前
已完结
Clinical Pharmacology Considerations on Recombinant Adeno‐Associated Virus–Based Gene Therapy
11天前
已完结
Pharmacokinetics, Biodistribution, Immunogenicity, and Model-Informed-Based PK/PD Model of a Next-Generation Advanced Novel Gene Therapy for Hemophilia
11天前
已完结
Practical guide to concentration-QTc modeling: a hands-on tutorial
17天前
已完结
Scientific rationale for a higher dose of nusinersen
1个月前
已完结
Population Pharmacokinetics of Nusinersen in the Cerebral Spinal Fluid and Plasma of Pediatric Patients With Spinal Muscular Atrophy Following Intrathecal Administrations
1个月前
已完结