Lv45
606 积分 2023-03-22 加入
Protein-based masks to unlock conditional activation of therapeutics
4小时前
已完结
AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by biallelic CBLN1 variants
4小时前
已完结
Solute carrier membrane transporters: emerging targets in CNS disorders
7天前
已完结
mRNA medicine for cardiovascular disease
13天前
已完结
Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors
15天前
已完结
Functional redundancy as a therapeutic strategy for genetic hearing loss
17天前
已完结
Design, simulate, refine: simulation-guided clinical trials for accelerated drug development
1个月前
已完结
Identification of a therapeutic threshold for AAV-STXBP1 gene therapy in a rodent model of STXBP1 developmental and epileptic encephalopathy
1个月前
已关闭
Defining therapeutic thresholds for STXBP1 gene therapy: From gene delivery to network rescue in neurodevelopmental disorders
1个月前
已关闭
T cell stemness and dysfunction in tumors are triggered by a common mechanism
1个月前
已完结