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116 积分 2022-02-17 加入
Dual Adeno-Associated Virus Vectors Result in Efficient In Vitro and In Vivo Expression of an Oversized Gene, MYO7A
1个月前
已关闭
Partial correction of endogenous ΔF508 CFTR in human cystic fibrosis airway epithelia by spliceosome-mediated RNA trans-splicing
1个月前
已完结
Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors
1个月前
已完结
AI-generated MLH1 small binder improves prime editing efficiency
7个月前
已完结