Lv1
30 积分 2024-02-23 加入
GFAP promoter elements required for region-specific and astrocyte-specific expression
21天前
已完结
AAV gene therapy for homozygous familial hypercholesterolemia: a phase 1 trial
1个月前
已完结
Transferrin and transferrin receptor function in brain barrier systems
3个月前
已完结
252. Using Cre-Dependent In Vivo Selection to Identify AAV Variants That Enable Efficient and Widespread Gene Transfer to the Adult Central Nervous System
3个月前
已完结
Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain
3个月前
已完结
Woodchuck hepatitis virus post-transcriptional regulatory element deleted from X protein and promoter sequences enhances retroviral vector titer and expression
3个月前
已完结
Potential oncogene activity of the woodchuck hepatitis post-transcriptional regulatory element (WPRE)
3个月前
已完结
Selection of appropriate non-clinical animal models to ensure translatability of novel AAV-gene therapies to the clinic
5个月前
已完结
Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain
8个月前
已完结
Model‐Informed Approach Supporting Drug Development and Regulatory Evaluation for Rare Diseases
8个月前
已完结