Lv1
30 积分 2024-05-20 加入
Exploring copy number variations in Lebanese families with rod-cone dystrophy reveals a novel deletion in PRPF31 with haploinsufficiency
1个月前
已完结
Gene Therapy with covalently-closed-end AAV vector for Spinal Muscular Atrophy
2个月前
已完结
Toxicologic Pathology Forum Opinion: Rational Approaches to Expanded Neurohistopathology Evaluation for Nonclinical General Toxicity Studies and Juvenile Animal Studies
2个月前
已完结
Generation of Induced-Primary Retinal Pigment Epithelium from Human Retinal Organoids
3个月前
已完结
Model‐Informed Approaches and Innovative Clinical Trial Design for Adeno‐Associated Viral Vector‐Based Gene Therapy Product Development: A White Paper
3个月前
已完结
Multiplex Immunofluorescence Assays
3个月前
已关闭
Gene therapy for neovascular age-related macular degeneration by subretinal delivery of RGX-314: a phase 1/2a dose-escalation study
4个月前
已完结
Gene therapy for neovascular age-related macular degeneration by subretinal delivery of RGX-314: a phase 1/2a dose-escalation study
4个月前
已完结
Disease progression of retinitis pigmentosa caused by PRPF31 variants in a Nordic population: a retrospective study with up to 36 years follow-up
4个月前
已完结
Span poly-L-arginine nanoparticles are efficient non-viral vectors for PRPF31 gene delivery: An approach of gene therapy to treat retinitis pigmentosa
5个月前
已关闭
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