Lv1
10 积分 2025-07-30 加入
Liver-Directed Molecular Therapies
3个月前
已完结
Treatment of a metabolic liver disease by in vivo genome base editing in adult mice
3个月前
已完结
In vivo base editing gene therapy for heterozygous familial hypercholesterolemia: a phase 1 trial
3个月前
已完结
Prime assembly with linear DNA donors enables large genomic insertions
3个月前
已完结
Prime editing using CRISPR-Cas12a and circular RNAs in human cells
3个月前
已完结
Programmable deletion, replacement, integration and inversion of large DNA sequences with twin prime editing
3个月前
已完结
Non-viral intron knock-ins for targeted gene integration into human T cells and for T-cell selection
4个月前
已完结
Quadruple pegRNA enables programmable and efficient large genomic insertion
4个月前
已完结
应用CRISPR/Cas9技术构建Wilson病小鼠模型及其基因治疗研究
6个月前
已完结
A Fluorescent Reporter Mouse for In Vivo Assessment of Genome Editing with Diverse Cas Nucleases and Prime Editors
7个月前
已完结