Lv11
30 积分 2026-03-17 加入
IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies
8小时前
待确认
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase
8小时前
已完结
Advances in Pompe Disease Treatment: From Enzyme Replacement to Gene Therapy
6天前
已完结
Silver-Russell Syndrome: A Review
8天前
已完结
[Consensus on diagnosis and treatment of Silver-Russell syndrome (2025)]
8天前
已完结
Lysosome Targeting Chimeras (LYTACs) That Engage a Liver-Specific Asialoglycoprotein Receptor for Targeted Protein Degradation
9天前
已完结
Trivalent siRNA-Conjugates with Guanosine as ASGPR-Binder Show Potent Knock-Down In Vivo
15天前
已完结
Hepatocyte-Targeted Cyclic Peptide LYTACs for PCSK9 Degradation and LDL Cholesterol Metabolic Regulation
23天前
已完结
Trivalent siRNA-Conjugates with Guanosine as ASGPR-Binder Show Potent Knock-Down In Vivo
1个月前
已完结
Crystal Structure of the Carbohydrate Recognition Domain of the Human Macrophage Galactose C-Type Lectin Bound to GalNAc and the Tumor-Associated Tn Antigen
1个月前
已完结