Lv1
40 积分 2023-08-22 加入
Antisense oligonucleotide–mediated MSH3 suppression reduces somatic CAG repeat expansion in Huntington’s disease iPSC–derived striatal neurons
1个月前
已完结
Safety and efficacy of valbenazine for the treatment of chorea associated with Huntington's disease (KINECT-HD): a phase 3, randomised, double-blind, placebo-controlled trial
1个月前
已完结
Clinical Efficacy and Safety of the Intra-articular Injection of Autologous Adipose-Derived Mesenchymal Stem Cells for Knee Osteoarthritis: A Phase III, Randomized, Double-Blind, Placebo-Controlled Trial
3个月前
已完结
Amyotrophic lateral sclerosis caused by FUS mutations: advances with broad implications
8个月前
已完结
A phase 2 randomized trial with autologous polyclonal expanded regulatory T cells in children with new-onset type 1 diabetes
9个月前
已完结
Clinical Safety and Preliminary Efficacy of Regulatory T Cells for ALS
9个月前
已完结
Safety, tolerability, and pharmacokinetics of antisense oligonucleotide BIIB078 in adults with C9orf72-associated amyotrophic lateral sclerosis: a phase 1, randomised, double blinded, placebo-controlled, multiple ascending dose study
10个月前
已完结
Mitochondrial Donation and Preimplantation Genetic Testing for mtDNA Disease
1年前
已完结
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