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Antisense oligonucleotide–mediated MSH3 suppression reduces somatic CAG repeat expansion in Huntington’s disease iPSC–derived striatal neurons |
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期刊:Science Translational Medicine 作者:Emma L. Bunting; Jasmine Donaldson; Sarah A. Cumming; Jessica Olive; Elizabeth L Broom; et al 出版日期:2025-02-12 |
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(2025-6-4)