| 标题 |
Pharmacokinetics and pharmacodynamics of PTC518, an oral huntingtin lowering splicing modifier: A first-in-human study |
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| DOI | |
| 其它 |
期刊:Br J Clin Pharmacol 作者:Gao L, Bhattacharyya A, Beers B, Kaushik D, Bredlau AL, Kristensen A, Abd-Elaziz K, Grant R, Golden L, Kong R 出版日期:2024-08-18 |
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(2025-6-4)