| 标题 |
Identification Of a Therapeutic Threshold For AAV-STXBP1 Gene Therapy in a Rodent Model of STXBP1 Developmental & Epileptic Encephalopathy |
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| DOI | |
| 其它 |
期刊:Molecular Therapy 作者:Nicholas B. Gallo; John W. Annand; Pete Clarner; Brian Harvey; Elena Morozova; et al 出版日期:2026-03-24 |
| 求助人 | |
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(2025-6-4)