转甲状腺素
危险系数
医学
安慰剂
内科学
临床终点
置信区间
心肌病
胃肠病学
心脏病学
临床试验
心力衰竭
病理
替代医学
作者
Matthew J. Maurer,Jeffrey H. Schwartz,Balarama Gundapaneni,Perry Elliott,Giampaolo Merlini,Márcia Waddington‐Cruz,Arnt V. Kristen,Martha Grogan,Ronald Witteles,Thibaud Damy,Brian Drachman,Sanjiv J. Shah,Mazen Hanna,Daniel P. Judge,Alexandra I. Barsdorf,Peter M. Huber,Terrell A. Patterson,Steve Riley,Jennifer Schumacher,Michelle Stewart
标识
DOI:10.1056/nejmoa1805689
摘要
In patients with transthyretin amyloid cardiomyopathy, tafamidis was associated with reductions in all-cause mortality and cardiovascular-related hospitalizations and reduced the decline in functional capacity and quality of life as compared with placebo. (Funded by Pfizer; ATTR-ACT ClinicalTrials.gov number, NCT01994889 .).
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