Phase 1 Trial of CRISPR-Cas9 Gene Editing Targeting ANGPTL3
作者
Luke J. Laffin,Stephen J. Nicholls,Russell Scott,Peter Clifton,John E. Baker,Ashish Sarraju,Shweta Singh,Qiuqing Wang,Kathy Wolski,Huansheng Xu,Jen Nielsen,Nipam H. Patel,Jason M. Duran,Steven E. Nissen
Editing of ANGPTL3 was associated with few adverse events and resulted in reductions from baseline in ANGPTL3 levels. (Funded by CRISPR Therapeutics; Australia New Zealand Clinical Trials Registry number, ACTRN12623000809639.).