赫拉
小分子
神经母细胞瘤RAS病毒癌基因同源物
突变体
GTP'
克拉斯
化学
生物化学
GTP酶
细胞生物学
水解
酶
基因
定向进化
生物
核苷酸
酶激活剂
HEK 293细胞
残留物(化学)
水解酶
作者
Yecheng Wang,Si‐Cong Chen,Yang Cao,Yang Wu,施仲达,Celine Wang,Michael A. Norinskiy,Hasan Celik,Ziyang Zhang
标识
DOI:10.1038/s41589-026-02291-1
摘要
The RAS family of oncogenes (KRAS, HRAS, NRAS) is among the most frequently mutated genes in human cancer. Therapeutic development has largely focused on inhibitors for KRAS codon 12 mutations, while mutant-selective inhibitors for Q61 variants remain elusive. A common mechanistic feature of G12 and Q61 mutants is the reduced efficiency of GTP hydrolysis, which enriches RAS in its active, signaling-competent state. Here we report small molecules that accelerate GTP hydrolysis in KRAS-Q61 mutants as an alternative therapeutic strategy. These compounds compensate for the loss of the catalytic residue Gln61 by introducing a general base into the active site, selectively enhancing hydrolysis of KRAS-Q61X (X = H, L, K, R) mutants by up to 20-fold. In mutant cancer cell lines, these compounds reduce GTP-bound RAS levels and suppress downstream signaling. This work establishes a mechanistic foundation for small-molecule 'GTPase activators' and offers a new paradigm for targeting RAS-driven cancers.
科研通智能强力驱动
Strongly Powered by AbleSci AI