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An AAV variant selected through NHP screens robustly transduces the brain and drives secreted protein expression in NHPs and mice |
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期刊:Science Translational Medicine 作者:Luis Tecedor; Yong Hong Chen; David E. Leib; Paul T. Ranum; Megan S. Keiser; et al 出版日期:2025-05-14 |
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(2025-6-4)