| 标题 |
Efficacy and safety of mitapivat in adults with transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial |
| 网址 | |
| DOI | |
| 其它 |
期刊:Lancet 作者:Cappellini MD, Sheth S, Taher A, Al-Samkari H, Antmen AB, Beneitez D, Cannas G, Coates T, Czapla L, Dahlin JL, Estepp JH, Feenstra E, Georgiev P, Gheuens S, Price GM, Glenthøj A, Musallam KM, Osman K, Porter JB, Shao H, Uhlig K, van Beers EJ, Viprakasit V, Kuo KHM, Kattamis A, ENERGIZE-T Investigators 出版日期:2026-09-01 |
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(2025-6-4)