| 标题 |
Intracerebroventricular SPAST-AAV9 gene therapy prevents the manifestation of symptoms in a mouse model of SPG4 Hereditary Spastic Paraplegia |
| 网址 | |
| DOI | |
| 其它 |
期刊:Molecular Therapy 作者:Emanuela Piermarini; Shrobona Guha; Liang Qiang; Heather Gray-Edwards; Miguel Sena-Esteves; et al 出版日期:2025-11-01 |
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(2025-6-4)