| 标题 |
A phase 2a study with SPL84: A novel RNA-targeted approach to restore CFTR function in people with CF carrying the 3849+10 kb C→T mutation |
| 网址 | |
| DOI |
10.1183/13993003.00866-2026
doi
|
| 其它 |
期刊:European Respiratory Journal 作者:Szczepan Cofta; Daria Springer; Kęstutis Malakauskas; Virginija Kalinauskaitė-Žukauskė; Karen McCoy; et al 出版日期:2026-10-15 |
| 求助人 | |
| 下载 |
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(2025-6-4)