| 标题 |
Adeno-Associated Virus Vectors: Principles, Practicesand Prospects in Gene Therapy
腺相关病毒载体：基因治疗的原理、实践与展望
|
| 网址 |
求助人暂未提供
|
| DOI |
暂未提供，该求助的时间将会延长，查看原因？
|
| 其它 |
Abstract Gene therapy offers promising potential as an efficacious and long-lasting therapeutic option for genetic conditions, by correcting defective mutations using engineered vectors to deliver genetic material to host cells. Among these vectors, adeno-associated viruses (AAVs) stand out for their efficiency, versatility, and safety, making them one of the leading platforms in gene therapy. The enormous potential of AAVs has been demonstrated through their use in over 225 clinical trials and the FDA’s approval of six AAV-based gene therapy products, positioning these vectors at the forefront of the field. This review highlights the evolution and current applications of AAVs in gene therapy, focusing on their clinical successes, ongoing developments, and the manufacturing processes required for the rapid commercial growth anticipated in the AAV therapy market. |
| 求助人 | |
| 下载 |
PDF的下载单位、IP信息已删除
(2025-6-4)
无极微光
凌凌
cdercder
Nole
v0id
xing_xing
水煮电吹风
欧克
DW
Kao
学术文献互助
GingerF
OK
DOC_XIONG
唠叨的大门
殷勤的紫槐
谢雷XIELei
认真芷容
Criminology34
潇洒的惋清
皖公网安备34019202002308
