| 标题 |
Safety, tolerability, and pharmacokinetics of antisense oligonucleotide BIIB078 in adults with C9orf72-associated amyotrophic lateral sclerosis: a phase 1, randomised, double blinded, placebo-controlled, multiple ascending dose study |
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| DOI | |
| 其它 |
期刊:Lancet Neurology 作者:Leonard H. van den Berg; Jeffrey D. Rothstein; Pamela J. Shaw; Suma Babu; Michael Benatar; et al 出版日期:2024-07-23 |
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(2025-6-4)