医学
内科学
中止
不利影响
靶向治疗
托法替尼
胃肠病学
类风湿性关节炎
癌症
作者
Jérôme Hadjadj,Yann Nguyen,Dalila Mouloudj,R. Bourguiba,Maël Heiblig,Hassina Aloui,Chloé McAvoy,Valentin Lacombe,Samuel Ardois,Corrado Campochiaro,Alexandre Maria,Cyrille Coustal,Thibault Comont,Estibaliz Lazaro,François Lifermann,G. Le Guenno,Hervé Lobbes,Vincent Grobost,R. Outh,J. Campagne
标识
DOI:10.1136/ard-2024-225640
摘要
Vacuoles, E1 enzyme, X-linked, autoinflammatory and somatic (VEXAS) syndrome is an adult-onset autoinflammatory disease associated with somatic ubiquitin-like modifier-activating enzyme 1 (UBA1) mutations. We aimed to evaluate the efficacy and safety of targeted therapies.
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