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Timed function tests have withstood the test of time as clinically meaningful and responsive endpoints in duchenne muscular dystrophy

医学 肌营养不良 杜氏肌营养不良 临床神经学 家庭医学 内科学 神经科学 心理学
作者
Craig M. McDonald
出处
期刊:Muscle & Nerve [Wiley]
卷期号:58 (5): 614-617 被引量:8
标识
DOI:10.1002/mus.26334
摘要

Muscle & NerveVolume 58, Issue 5 p. 614-617 Editorial Timed function tests have withstood the test of time as clinically meaningful and responsive endpoints in duchenne muscular dystrophy Craig M. McDonald MD, Corresponding Author Craig M. McDonald MD cmmcdonald@ucdavis.edu Department of Physical Medicine & Rehabilitation, University of California, Davis School of Medicine, Sacramento, California, USACorrespondence to: C.M. McDonald; e-mail: cmmcdonald@ucdavis.eduSearch for more papers by this author Craig M. McDonald MD, Corresponding Author Craig M. McDonald MD cmmcdonald@ucdavis.edu Department of Physical Medicine & Rehabilitation, University of California, Davis School of Medicine, Sacramento, California, USACorrespondence to: C.M. McDonald; e-mail: cmmcdonald@ucdavis.eduSearch for more papers by this author First published: 07 September 2018 https://doi.org/10.1002/mus.26334Citations: 2 See article on pages 631–638, in this issue. Funding: : United States Department of Education; NIDRR; NIDILRR; NIH/NIAMS; United States Department of Defense; Parent Project Muscular Dystrophy Conflicts of Interest: : C.M.M. has served as a consultant for clinical trials for PTC Therapeutics, Biomarin, Sarepta Therapeutics, Eli Lilly, Pfizer, Santhera Pharmaceuticals, Cardero Therapeutics, Inc., Catabasis, Capricor Therapeutics, Astellas, and Mitobridge; and currently serves on external advisory boards related to Duchenne muscular dystrophy for PTC Therapeutics, Eli Lilly, Sarepta Therapeutics, Santhera Pharmaceuticals, and Capricor. Read the full textAboutPDF ToolsRequest permissionExport citationAdd to favoritesTrack citation ShareShare Give accessShare full text accessShare full-text accessPlease review our Terms and Conditions of Use and check box below to share full-text version of article.I have read and accept the Wiley Online Library Terms and Conditions of UseShareable LinkUse the link below to share a full-text version of this article with your friends and colleagues. Learn more.Copy URL Share a linkShare onFacebookTwitterLinked InRedditWechat Citing Literature Volume58, Issue5November 2018Pages 614-617 RelatedInformation

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